A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease
Recruiting · NCT07354724 · Registry updated 2026-08-17Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study to Evaluate the Safety, Pharmacokinetics, and Pharmacodynamics of DNL952 in Adult Participants With Late-Onset Pompe Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder | Recruiting | Phase 1 | 2026-08-17 | NCT07354724 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Denali Therapeutics Inc. | 9 |
4 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Duke University School of Medicine - Early Phase Research Unit | Durham | United States | 1 |
| The Lysosomal & Rare Disorders Research & Treatment Center | Fairfax | United States | 1 |
| University of California-Irvine | Irvine | United States | 1 |
| Washington University School of Medicine | St Louis | United States | 895 |