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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypotension, Orthostatic, Menkes disease, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, X-linked disease, autonomic nervous system disorder, brain disorder, cardiovascular disorder, central nervous system disorder, disorder of pilosebaceous unit, hereditary disease, hypotensive disorder, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorder, orthostatic intolerance, primary dysautonomia, skin disorder, vascular disorderRecruitingPhase 1 / Phase 22026-10-05NCT07398508

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OrganizationsLinked trials
Stephen G. Kaler1

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Research sitesCityCountryLinked trials
Vagelos College of Physicians and Surgeons, Columbia UniversityNew YorkUnited States1