NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes Disease
NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes Disease
Recruiting · NCT07398508 · Registry updated 2026-10-05Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| NORTHERA (DROXIDOPA) for Dysautonomia in Pediatric Survivors of Menkes Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hypotension, Orthostatic, Menkes disease, Neurobehavioral Manifestations, Neurologic Manifestations, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, X-linked disease, autonomic nervous system disorder, brain disorder, cardiovascular disorder, central nervous system disorder, disorder of pilosebaceous unit, hereditary disease, hypotensive disorder, inborn errors of metabolism, inborn metal metabolism disorder, inherited neurodegenerative disorder, intellectual disability, metabolic disease, nervous system disorder, orthostatic intolerance, primary dysautonomia, skin disorder, vascular disorder | Recruiting | Phase 1 / Phase 2 | 2026-10-05 | NCT07398508 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Stephen G. Kaler | 1 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Vagelos College of Physicians and Surgeons, Columbia University | New York | United States | 1 |