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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Phase 1b Study of Adenylosuccinic Acid (ASA-001) for Adenylosuccinate Synthase 1 (ADSS1) Deficient Myopathy.Adenylosuccinate Synthase 1 Deficient MyopathyEnrolling by invitationPhase 12026-04-07NCT07412821

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Research sitesCityCountryLinked trials
University of California Los Angeles (UCLA)Los AngelesUnited States11