Personalized Antisense Oligonucleotide for A Single Participant With PACS1 Gene Mutation Associated With Schuurs-Hoeijmakers Syndrome (SHMS)
Personalized Antisense Oligonucleotide for A Single Participant With PACS1 Gene Mutation Associated With Schuurs-Hoeijmakers Syndrome (SHMS)
Not yet recruiting · NCT07474298 · Registry updated 2026-03-16Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Personalized Antisense Oligonucleotide for A Single Participant With PACS1 Gene Mutation Associated With Schuurs-Hoeijmakers Syndrome (SHMS) | Schuurs-Hoeijmakers syndrome | Not yet recruiting | Phase 1 / Phase 2 | 2026-03-16 | NCT07474298 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| n-Lorem Foundation | 18 |
| The Hospital for Sick Children | 162 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| The Hospital for Sick Children (SickKids) | Toronto | Canada | 9 |