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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Safety and Preliminary Efficacy of TSHA-102 Gene Therapy in Pediatric Females Aged >2 to <4 Years With Rett SyndromeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rett syndrome, Signs and Symptoms, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorderActive, not recruitingPhase 32026-08-19NCT07480564

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OrganizationsLinked trials
Taysha Gene Therapies, Inc.4

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Research sitesCityCountryLinked trials
Boston Children's HospitalBostonUnited States343
Rush University Medical CenterChicagoUnited States283
University of Alabama at BirminghamBirminghamUnited States193