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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, Myotonia, Neurologic Manifestations, Neuromuscular Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic dystrophy type 1, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseRecruitingPhase 32026-10-05NCT07486934

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OrganizationsLinked trials
Dyne Therapeutics7

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Research sitesCityCountryLinked trials
Aarhus University Hospital, Department of NeurologyAarhusDenmark1
AP-HP, Hôpital Raymond-PoincaréGarchesFrance1
Azienda Ospedaliero-Universitaria Sant'Andrea - UOC NeurologiaRomaItaly1
Centro Clinico Nemo Brescia, Fondazione Serena ETSGussagoItaly1
Centro Clinico Nemo Milano, Fondazione Serena ETSMilanItaly1
Charité Universitätsmedizin Berlin Campus-Buch Muscle Research UnitBerlinGermany1
CHU de Nantes - Hôtel-DieuNantesFrance1
CHU de Toulouse - Hôpital Pierre-Paul RiquetToulouseFrance1
CHU Marseille - Hôpital de la Timone (APHM)MarseilleFrance1
Fondazione Policlinico Universitario A. Gemelli IRCCS - Department of Women's, Child and Public Health Sciences - UOC Neuropsichiatria InfantileRomaItaly1
Hospital Universitario Infanta SofíaSan Sebastián de los ReyesSpain5
Houston Methodist Neurological InstituteHoustonUnited States18
IU Health Neuroscience CenterIndianapolisUnited States7
Kennedy Krieger InstituteBaltimoreUnited States41
LMU Klinikum der Universität München Neurologische Klinik und Poliklinik Friedrich-Baur-Institut Campus InnenstadtMunichGermany1
National Center Hospital, National Center of Neurology and Psychiatry (NCNP)KodairaJapan1
National Hospital Organization Osaka Toneyama Medical CenterToyonaka-ShiJapan2
Niigata National Hospital, National Hospital OrganizationKashiwazakiJapan1
Northern Care Alliance NHS Foundation TrustSalfordUnited Kingdom1
Pitié-Salpêtrière HospitalParisFrance7
Radboud University Medical CenterNijmegenNetherlands15
Rare Disease Research, LLCHillsboroughUnited States2
Rare Disease Research, LLCAtlantaUnited States8
Rigshospitalet, (Neuromuscular Clinic and Research Unit, Department 8077)CopenhagenDenmark1
Roy Blunt NextGen Precision Health InstituteColumbiaUnited States1