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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
AAVrh10-PCCA Gene Therapy for Propionic AcidemiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, propionic acidemiaRecruitingPhase 12026-08-21NCT07643844

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OrganizationsLinked trials
Mayo Clinic970

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Research sitesCityCountryLinked trials
Mayo ClinicRochesterUnited States664