AAVrh10-PCCA Gene Therapy for Propionic Acidemia
AAVrh10-PCCA Gene Therapy for Propionic Acidemia
Recruiting · NCT07643844 · Registry updated 2026-08-21Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| AAVrh10-PCCA Gene Therapy for Propionic Acidemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, propionic acidemia | Recruiting | Phase 1 | 2026-08-21 | NCT07643844 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Mayo Clinic | 970 |
1 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Mayo Clinic | Rochester | United States | 664 |