Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)
Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)
Not yet recruiting · NCT07681713 · Registry updated 2026-08-14Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorder | Not yet recruiting | Phase 3 | 2026-08-14 | NCT07681713 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| PTC Therapeutics | 8 |
9 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Centre Hospitalier de l'Universite de Montreal CHUM | Montreal | Canada | 1 |
| Children's Hospital of Philadelphia | Philadelphia | United States | 434 |
| Hospital Sant Joan de Deu | Barcelona | Spain | 11 |
| Hôpital Érasme (Hôpital Universitaire de Bruxelles) | Brussels | Belgium | 1 |
| Institut du Cerveau et de la Moelle Epinière | Paris | France | 1 |
| University of California Los Angeles | Los Angeles | United States | 87 |
| University of Campinas | Campinas | Brazil | 1 |
| University of Iowa | Iowa City | United States | 284 |
| University of South Florida | Tampa | United States | 73 |