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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Term Efficacy Study of Vatiquinone for the Treatment of Friedreich's Ataxia (FA)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorderNot yet recruitingPhase 32026-08-14NCT07681713

1 results · Page 1 of 1

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OrganizationsLinked trials
PTC Therapeutics8

9 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Centre Hospitalier de l'Universite de Montreal CHUMMontrealCanada1
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Hospital Sant Joan de DeuBarcelonaSpain11
Hôpital Érasme (Hôpital Universitaire de Bruxelles)BrusselsBelgium1
Institut du Cerveau et de la Moelle EpinièreParisFrance1
University of California Los AngelesLos AngelesUnited States87
University of CampinasCampinasBrazil1
University of IowaIowa CityUnited States284
University of South FloridaTampaUnited States73