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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
MPS IIIA Disease Monitoring ProgramCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Mucopolysaccharidosis III, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 3ANot yet recruitingNot stated2026-10-02NCT07855562

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OrganizationsLinked trials
Ultragenyx Pharmaceutical Inc24

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