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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study of Zipalertinib in Patients With Advanced Non-Small Cell Lung Cancer With Epidermal Growth Factor Receptor (EGFR) Exon 20 Insertions or Other Uncommon Mutation.Neoplasms by Histologic Type, carcinoma, epithelial neoplasm, lung disorder, neoplasm, respiratory system disorderRecruitingPhase 22026-10-06NCT05967689
A Multi-phase Study of ASTX030 (Azacitidine and Cedazuridine) in Myeloid Neoplasm Alone or in Combination With Venetoclax in AML (AZTOUND Study)Chronic Disease, Disease Attributes, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Pathologic Processes, Pathological Conditions, Signs and Symptoms, acute myeloid leukemia, anemia, bone marrow disorder, chronic myelomonocytic leukemia, hematologic disorder, leukemia, myelodysplastic syndrome, myelodysplastic syndrome with excess blasts, myelodysplastic syndrome with single lineage dysplasia, myelodysplastic/myeloproliferative disease, myeloid leukemia, neoplasmRecruitingPhase 2 / Phase 32026-10-06NCT04256317
A Study to Learn About the Study Medicine Aztreonam-Avibactam (ATM-AVI) in Infants and Newborns Admitted in Hospitals With Bacterial Infection (CHERISH)Bacterial Infections and Mycoses, Infections, bacterial infectious disease, gram-negative bacterial infectionsRecruitingPhase 22026-09-24NCT06462235
Adjuvant Therapy in POLE-Mutated and p53-Wildtype/NSMP Early Stage Endometrial Cancer RAINBO BLUE & TAPERFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Genital Diseases, Neoplasms by Site, Urogenital Diseases, Urogenital Neoplasms, endometrium neoplasm, female reproductive system disorder, female reproductive system neoplasm, neoplasm, uterine disorderRecruitingPhase 22026-09-24NCT05640999
A Study of Vosoritide in Children With Noonan Syndrome With Inadequate Growth During or After Human Growth Hormone TreatmentBone Diseases, Developmental, Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Craniofacial Abnormalities, Dwarfism, Musculoskeletal Abnormalities, Noonan syndrome, Skin and Connective Tissue Diseases, bone disorder, cardiovascular disorder, congenital heart disease, connective tissue disorder, endocrine system disorder, heart disorder, hereditary disease, musculoskeletal system disorderActive, not recruitingPhase 22026-09-23NCT06668805
A Study to Compare Elritercept With Epoetin Alfa to Treat Anemia in Adults With Very Low, Low, or Intermediate Risk Myelodysplastic Syndromes (MDS) Who Need Regular Blood TransfusionsHemic and Lymphatic Diseases, anemia, bone marrow disorder, hematologic disorder, myelodysplastic syndromeRecruitingPhase 32026-09-18NCT07422480
A Study Investigating Intravenous Human Normal Immunoglobulin 10% in Adults With Chronic Immune Thrombocytopenia (ITP)Cytopenia, Hemic and Lymphatic Diseases, Hemorrhage, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Purpura, Thrombocytopenic, Idiopathic, Signs and Symptoms, Skin Manifestations, autoimmune disease, blood coagulation disease, blood platelet disease, hematologic disorder, hemorrhagic disease, immune system disorder, purpura, thrombocytopenia, thrombocytopenic purpura, thrombotic microangiopathyRecruitingPhase 32026-09-11NCT07059000
An Open-Label Study to Evaluate the Long-Term Safety and Efficacy of ALXN2220 in Adults With Transthyretin Amyloid CardiomyopathyTransthyretin Amyloid Cardiomyopathy (ATTR-CM)Not yet recruitingPhase 32026-08-28NCT07789483
A Study of Roginolisib in Combination With Ruxolitinib in Patients With Myelofibrosis (MF) Who Are Unresponsive to JAK InhibitorsHemic and Lymphatic Diseases, Myeloproliferative Disorders, bone marrow disorder, hematologic disorder, primary myelofibrosisRecruitingPhase 1 / Phase 22026-06-23NCT06887803
RimegepAnt effectIvenesS and tolErability as Migraine Preventive TreatmentHeadache, Headache Disorders, Secondary, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, headache disorder, hypnic headache, migraine disorder, migraine with aura, migraine without aura, nervous system disorderRecruitingNot stated2026-06-11NCT06409832
A Phase 2 Study of Vosoritide in Children With Idiopathic Short StatureIdiopathic Short StatureRecruitingPhase 22026-05-22NCT06382155
Study of the Kono-S Anastomosis Versus the Side-to-side Functional End AnastomosisCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderRecruitingNot applicable2026-05-14NCT03256240
Study on 30 Outpatients With Chronic Migraine Treated With Well-Being Therapy or With a Control TherapyBronchiolitis Obliterans, brain disorder, bronchial disorder, bronchiolitis, bronchiolitis obliterans syndrome, bronchitis, central nervous system disorder, cryptogenic organizing pneumonia, graft versus host disease, headache disorder, hypnic headache, immune system disorder, lung disorder, migraine disorder, nervous system disorder, obstructive lung disease, respiratory system disorderRecruitingNot applicable2026-05-05NCT03404336
Preoperative vs Postoperative Hypofractionated Radiosurgery for Patients With Large Brain MetastasesNeoplasms by Site, brain disorder, central nervous system cancer, central nervous system disorder, neoplasm, nervous system disorderRecruitingNot applicable2026-04-30NCT05545007
A Phase 2 in Adult Subjects With Hereditary AngioedemaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Complement Deficiency Diseases, Hypersensitivity, Immediate, Primary Immunodeficiency Diseases, Skin and Connective Tissue Diseases, angioedema, cardiovascular disorder, hereditary angioedema, hereditary disease, immune system disorder, inborn error of immunity, skin disorder, skin vascular disease, urticaria, vascular disorderActive, not recruitingPhase 22026-04-17NCT06846398
Outcomes in ARMs: Comparison Between Surgical Techniques in Patients With Perineal or Vestibular Fistula - a Multicenter Italian StudyAnorectal Malformations, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System DiseasesRecruitingNot stated2026-03-27NCT07438691
Neonatal Intestinal Obstruction: Prenatal Factors and Postnatal OutcomesDigestive System Diseases, digestive system disorder, intestinal disorder, intestinal obstructionRecruitingNot stated2026-02-25NCT07434596
TED_ORG: Study on Short Bowel SyndromeDigestive System Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, digestive system disorder, intestinal disorder, malabsorption syndrome, short bowel syndromeRecruitingNot applicable2026-02-10NCT07400783
KETO-TUMOR: a Study on Brain Tumors and Central ObesityNeoplasms by Site, brain disorder, central nervous system cancer, central nervous system disorder, hypothalamic disorder, hypothalamic neoplasm, neoplasm, nervous system disorder, supratentorial cancerRecruitingNot applicable2026-02-09NCT07396896
Clinical, Biochemical and Epigenetic Profile of Pediatric Behçet DiseaseBehcet disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Skin and Connective Tissue Diseases, Stomatognathic Diseases, anterior uveitis, cardiovascular disorder, eye disorder, hereditary disease, hereditary periodic fever syndrome, hereditary skin disorder, mouth disorder, panuveitis, skin disorder, skin vascular disease, uveal disorder, uveitis, vascular disorder, vasculitisRecruitingNot applicable2026-01-29NCT07375940
Open-Label Safety Study of Acoramidis (AG10) in Symptomatic ATTR ParticipantsAmyloid Neuropathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, amyloidosis, familial amyloid neuropathy, hereditary amyloidosis, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, proteostasis deficienciesActive, not recruitingPhase 32025-10-14NCT04988386
AggRegated System Of sensOrs and Multimedia Monitors: Technology for innovAtion and personalizaTion of rEhabilitation Care. (ROOMMATE)brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, nervous system disorder, stroke disorder, vascular disorderNot yet recruitingNot applicable2025-03-21NCT06728020