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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Investigate the Safety, Tolerability, and Pharmacokinetics of ATI-105 in Healthy AdultsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Mitochondrial Dysfunction, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, cardiomyopathy, cardiovascular disorder, central nervous system disorder, cerebellar disorder, heart disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorderNot yet recruitingPhase 12026-10-09NCT07869654
Time Comparison of Interventions on Bowel Programs in Spinal Cord InjuryDigestive System Diseases, central nervous system disorder, colonic disorder, digestive system disorder, functional colonic disease, injury, intestinal disorder, nervous system disorder, nervous system injury, neurogenic bowel, spinal cord disorder, spinal cord injuryRecruitingNot applicable2026-10-09NCT07817199
A Study to Evaluate the Efficacy and Safety of Subcutaneous Nomlabofusp in Subjects With Friedreich's AtaxiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorderRecruitingPhase 32026-10-09NCT07778836
Interfacing With NeuroTechnology to Expand Neural Throughput (INTENT)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Infarction, Muscular Disorders, Atrophic, Necrosis, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, TDP-43 proteinopathy, amyotrophic lateral sclerosis, brain disorder, brain infarction, brain ischemia, brain stem infarction, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, injury, ischemic disease, metabolic disease, motor neuron disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, nervous system injury, neurodegenerative disease, neuromuscular disease, palsy, progressive muscular atrophy, proteostasis deficiencies, quadriplegia, spinal cord disorder, spinal cord injury, spinal muscular atrophy, stroke disorder, vascular disorderRecruitingNot applicable2026-10-09NCT07521930
Self-Efficacy Enhancement Among Online Support Group of Primary Caregivers of Children With Neuro Muscular DystrophyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, central nervous system disorder, hereditary disease, motor neuron disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyActive, not recruitingNot applicable2026-10-09NCT07356063
An Open-Label Study of CTI-1601 in Subjects With Friedreich's AtaxiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorderRecruitingPhase 22026-10-09NCT06447025
A Study to Assess the Safety, Tolerability, and Pharmacology of Darifenacin in Patients With ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingPhase 22026-10-09NCT06249867
Patterns of Rehabilitation After Spinal Cord Injurycentral nervous system disorder, injury, nervous system disorder, nervous system injury, spinal cord disorder, spinal cord injuryRecruitingNot stated2026-10-08NCT07865338
PhiCube for Bilateral Upper Limb Neuromotor and Cognitive Rehabilitation in AdultsCognition Disorders, Cognitive Dysfunction, Mild Cognitive Impairment, Neurologic Manifestations, Nutritional and Metabolic Diseases, Paresis, Parkinson disease, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, TDP-43 proteinopathy, Upper Extremity Paresis, amyotrophic lateral sclerosis, basal ganglia disorder, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, cognitive disorder, injury, metabolic disease, motor neuron disorder, movement disorder, nervous system disorder, nervous system injury, neurodegenerative disease, neuromuscular disease, parkinsonian disorder, proteostasis deficiencies, psychiatric disorder, spinal cord disorder, spinal cord injury, stroke disorder, synucleinopathy, vascular disorderNot yet recruitingNot applicable2026-10-08NCT07865260
Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy PatientsBacterial Infections and Mycoses, Central Nervous System Bacterial Infections, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Fatigue, Infections, Muscular Disorders, Atrophic, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Treponema infectious disease, X-linked disease, bacterial infectious disease, central nervous system disorder, central nervous system infectious disorder, gram-negative bacterial infections, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, neurosyphilis, spinal cord disorder, spirochaetales infections, syphilis, tabes dorsalisRecruitingPhase 22026-10-08NCT07766980
Do Video Recordings of Multidisciplinary Clinics Improve Quality of Life for People With ALS and Their Caregivers?Nutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingNot applicable2026-10-08NCT07454733
A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Administration of ARGX-119 in Pediatric Participants Aged 5 to Less Than 18 Years With Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyRecruitingPhase 22026-10-08NCT07287982
A Study of Risdiplam in Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophycentral nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophyActive, not recruitingPhase 22026-10-08NCT03779334
Evaluation and Treatment of Neurosurgical DisordersNeoplasms by Site, Parkinson disease, Pituitary Neoplasms, basal ganglia disorder, brain disorder, central nervous system cancer, central nervous system disorder, endocrine system disorder, epilepsy, hypothalamic disorder, hypothalamic neoplasm, malignant endocrine neoplasm, movement disorder, neoplasm, nervous system disorder, neurodegenerative disease, parkinsonian disorder, pituitary gland disorder, spinal cord disorder, spinal cord neoplasm, supratentorial cancer, synucleinopathyRecruitingNot stated2026-10-08NCT00060541
Conservative Care Versus Decompression Trial for Degenerative Cervical Myelopathy Pilotcentral nervous system disorder, nervous system disorder, spinal cord disorderNot yet recruitingNot applicable2026-10-07NCT07358273
ARTFL LEFFTDS Longitudinal Frontotemporal Lobar Degeneration (ALLFTD)Frontotemporal Lobar Degeneration, Neurologic Manifestations, Nutritional and Metabolic Diseases, Ocular Motility Disorders, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, TDP-43 proteinopathy, amyotrophic lateral sclerosis, basal ganglia disorder, brain disorder, central nervous system disorder, cognitive disorder, corticobasal degeneration disorder, cranial nerve neuropathy, dementia, eye disorder, frontotemporal dementia, frontotemporal dementia with motor neuron disease, metabolic disease, motor neuron disorder, movement disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, ophthalmoplegia, palsy, proteostasis deficiencies, psychiatric disorder, spinal cord disorder, tauopathyRecruitingNot stated2026-10-07NCT04363684
Thermal Ablation and Spine Stereotactic Radiosurgery in Treating Patients With Spine Metastases at Risk for Compressing the Spinal CordDigestive System Diseases, Digestive System Neoplasms, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Head and Neck Neoplasms, Male Urogenital Diseases, Neoplasm Metastasis, Neoplasms by Histologic Type, Neoplasms by Site, Neoplasms, Connective and Soft Tissue, Neoplasms, Germ Cell and Embryonal, Neoplasms, Nerve Tissue, Neoplasms, Unknown Primary, Neoplastic Processes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Skin and Connective Tissue Diseases, Spinal Cord Compression, Urogenital Diseases, Urogenital Neoplasms, adenocarcinoma, benign urinary system neoplasm, carcinoma, central nervous system disorder, digestive system cancer, digestive system disorder, digestive system neoplasm, endocrine system disorder, epithelial neoplasm, injury, kidney cancer, kidney disorder, malignant endocrine neoplasm, melanocytic neoplasm, melanoma, metastatic melanoma, neoplasm, nervous system disorder, neuroendocrine neoplasm, primitive neuroectodermal tumor, renal cell carcinoma, sarcoma, skin disorder, skin neoplasm, spinal cord disorder, spinal cord injury, thyroid gland carcinoma, thyroid gland disorder, thyroid tumor, urinary system disorderActive, not recruitingPhase 22026-10-07NCT02713269
VYVGART (Hytrulo) in Patients With Stiff Person Syndrome (SPS)autoimmune disease, autoimmune disorder of the nervous system, central nervous system disorder, immune system disorder, nervous system disorder, neuromuscular disease, spinal cord disorder, stiff-person syndromeRecruitingPhase 2 / Phase 32026-10-06NCT07860021
SERENITY Study of Chronic Pain Interference in AdultsChronic Pain, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, central nervous system disorder, injury, nervous system disorder, nervous system injury, neuralgia, neuromuscular disease, peripheral nervous system disorder, spinal cord disorder, spinal cord injuryNot yet recruitingNot stated2026-10-06NCT07820475
Pridopidine Phase 3 Study to Evaluate Efficacy and Safety in ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingPhase 32026-10-06NCT07322003
Testosterone and Neural Function in Men With Spinal Cord Injurycentral nervous system disorder, injury, nervous system disorder, nervous system injury, spinal cord disorder, spinal cord injuryRecruitingEarly phase 12026-10-06NCT06130449
Trial on the Biological and Clinical Effects of Acetyl-L-carnitine in ALSNutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorderRecruitingPhase 2 / Phase 32026-10-06NCT06126315
Biomarkers in Friedreich's AtaxiaCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyskinesias, Friedreich ataxia, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Spinocerebellar Degenerations, atactic disorder, non-human animal, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorderRecruitingNot stated2026-10-06NCT02497534
A Study to Learn About the Investigational Drug Rinzimetostat (ORIC-944) in Patients With mCRPC Who Were Previously Treated With Abiraterone Acetate (Himalayas-1)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Genital Diseases, Kennedy disease, Male Urogenital Diseases, Neoplasms by Site, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Recurrence, Urogenital Diseases, Urogenital Neoplasms, X-linked disease, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, male reproductive organ cancer, male reproductive system disorder, motor neuron disorder, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, prostate cancer, prostate disorder, spinal cord disorder, spinal muscular atrophyRecruitingPhase 32026-10-05NCT07723248
Glycemic and Weight Loss Effects of GLP-1R Agonist Therapy in Subjects With Spinal Cord Injury and Type 2 DiabetesNutritional and Metabolic Diseases, central nervous system disorder, diabetes mellitus, endocrine system disorder, glucose metabolism disease, injury, metabolic disease, nervous system disorder, nervous system injury, spinal cord disorder, spinal cord injury, type 2 diabetes mellitusRecruitingPhase 42026-10-05NCT06706284