Neurogene Inc.

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome	Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rett syndrome, Signs and Symptoms, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorder	Active, not recruiting	Phase 3	2026-06-10		NCT05898620
Gene Therapy Study for Children With CLN5 Batten Disease	Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative disease	Active, not recruiting	Phase 1 / Phase 2	2024-08-12		NCT05228145

Clinical trials