Gene Therapy Study for Children With CLN5 Batten Disease
Gene Therapy Study for Children With CLN5 Batten Disease
Active, not recruiting · NCT05228145 · Registry updated 2024-08-12Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Gene Therapy Study for Children With CLN5 Batten Disease | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Neuronal Ceroid-Lipofuscinoses, Nutritional and Metabolic Diseases, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, lysosomal lipid storage disorder, metabolic disease, nervous system disorder, neurodegenerative disease | Active, not recruiting | Phase 1 / Phase 2 | 2024-08-12 | NCT05228145 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Neurogene Inc. | 2 |
2 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Great Ormond Street Hospital for Children | London | United Kingdom | 24 |
| University of Rochester | Rochester | United States | 360 |