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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Clinical and Genetic Evaluation of Individuals With Undiagnosed Disorders Through the Undiagnosed Diseases NetworkCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Disease Attributes, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Rare Diseases, Undiagnosed Diseases, hereditary diseaseRecruitingNot stated2026-10-07NCT02450851
A Study of the Efficacy and Safety of Danicamtiv in Participants With Symptomatic Genetic and Familial Dilated CardiomyopathySymptomatic Genetic Dilated CardiomyopathyRecruitingPhase 2 / Phase 32026-10-05NCT07210723
A Study of the Long-term Safety and Efficacy of Danicamtiv in Adults With Symptomatic Genetic and Familial Dilated CardiomyopathySymptomatic Genetic Dilated Cardiomyopathy (DCM)RecruitingPhase 32026-10-02NCT07771465
Pivotal Study of the SUpira System in Patients Undergoing High-Risk Percutaneous COronaRy InTervention (HRPCI)Arterial Occlusive Diseases, arteriosclerosis disorder, cardiovascular disorder, coronary artery disorder, heart disorder, myocardial ischemia, vascular disorderRecruitingNot applicable2026-09-30NCT07296744
A Trial Comparing Unrelated Donor BMT With IST for Pediatric and Young Adult Patients With Severe Aplastic Anemia (TransIT, BMT CTN 2202)Bone Marrow Failure Disorders, Hemic and Lymphatic Diseases, anemia, aplastic anemia, bone marrow disorder, hematologic disorderActive, not recruitingPhase 32026-09-25NCT05600426
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseActive, not recruitingPhase 1 / Phase 22026-09-23NCT05481879
Long-term Follow-up of Patients Treated With Genetically Modified Autologous T CellsBlood Protein Disorders, Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, T-cell non-Hodgkin lymphoma, cardiovascular disorder, diffuse large B-cell lymphoma, hematologic disorder, hemorrhagic disease, immune system disorder, immunoproliferative disorder, lymphatic system disorder, lymphoma, lymphoproliferative syndrome, monoclonal gammopathy, neoplasm, plasma cell neoplasm, vascular disorder, vascular hemostatic diseaseEnrolling by invitationPhase 22026-09-22NCT03628612
Belimumab With Rituximab for Primary Membranous NephropathyFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, autoimmune disease, glomerulonephritis, immune system disorder, kidney disorder, membranous glomerulonephritis, nephritis, nephrosis, nephrotic syndrome, urinary system disorderRecruitingPhase 22026-09-18NCT03949855
IT Matters: The Erectile Restoration RegistryGenital Diseases, Male Urogenital Diseases, Sexual Dysfunctions, Psychological, Urogenital Diseases, erectile dysfunction, male reproductive system disorder, physiological sexual disorder, psychiatric disorderEnrolling by invitationNot stated2026-09-14NCT04200937
Surveillance vs. Endoscopic Therapy for Barrett's Esophagus With Low-grade DysplasiaBarrett esophagus, Digestive System Diseases, digestive system disorder, esophageal adenocarcinoma, esophageal disorder, neoplasm, precancerous conditionRecruitingNot applicable2026-09-11NCT05753748
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory CohortCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingPhase 12026-09-11NCT04626674
Personalized Reduction of Chemotherapy Intensity Through ctDNA Evaluation for the Treatment of Patients With Advanced Hodgkin Lymphomaclassic Hodgkin lymphomaRecruitingPhase 22026-09-09NCT06745076
Daily Adaptive Radiation Therapy Using an Individualized Approach for Prostate CancerGenital Diseases, Male Urogenital Diseases, Neoplasms by Site, Urogenital Diseases, Urogenital Neoplasms, male reproductive organ cancer, male reproductive system disorder, neoplasm, prostate cancer, prostate disorderRecruitingNot applicable2026-09-09NCT05804318
Building a Renewed ImaGe After Head & Neck Cancer Treatment (BRIGHT) Multi-Site RCTHead and Neck Neoplasms, Neoplasms by Site, head and neck cancer, neoplasmRecruitingNot applicable2026-09-04NCT05442957
Domatinostat With Sirolimus for Relapsed, Refractory Sarcoma and OsteosarcomaNeoplasms by Histologic Type, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, neoplasm, osteosarcoma, sarcomaRecruitingPhase 1 / Phase 22026-09-03NCT07725380
RESEARCH EVALUATING VAGAL EXCITATION AND ANATOMICAL LINKSbrain disorder, central nervous system disorder, depressive disorder, epilepsy, mood disorder, nervous system disorder, psychiatric disorderActive, not recruitingNot applicable2026-09-03NCT06143293
Assessment of Chimerism and Relapse Post Bone Marrow/Hematopoietic Cell Transplant (HCT) Using AlloHeme TestHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, acute myeloid leukemia, bone marrow disorder, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, myelodysplastic syndrome, myeloid leukemia, neoplasmActive, not recruitingNot stated2026-09-03NCT04635384
Prevention/Reduction of ASRs and PTSD to Sustain Civilian Performance With Sublingual Cyclobenzaprine HCl (TNX-102 SL)Stress Disorders, Traumatic, Stress Disorders, Traumatic, Acute, acute stress disorder, psychiatric disorderRecruitingPhase 22026-09-01NCT06636786
Clinical Trial of Inhaled Molgramostim Nebulizer Solution in Autoimmune Pulmonary Alveolar Proteinosis (aPAP)autoimmune pulmonary alveolar proteinosisActive, not recruitingPhase 32026-08-26NCT04544293
Transauricular Vagus Nerve Stimulation in ChildrenHypoxia, Hypoxia, Brain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Respiratory, brain disorder, brain hypoxia - ischemia, brain ischemia, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, nervous system disorder, vascular disorderEnrolling by invitationNot applicable2026-08-25NCT06168071
Group Versus Traditional Prenatal Care for DiabetesFemale Urogenital Diseases and Pregnancy Complications, Nutritional and Metabolic Diseases, Urogenital Diseases, diabetes mellitus, endocrine system disorder, gestational diabetes, glucose metabolism disease, metabolic disease, pregnancy disorder, type 2 diabetes mellitusActive, not recruitingNot applicable2026-08-21NCT03301792
Cerebrovascular Reactivity Measurements With High-Density Diffuse Optical TomographyCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, nervous system disorder, sickle cell disease, stroke disorder, vascular disorderRecruitingNot applicable2026-08-20NCT07776444
Ultrasonic Neuromodulation of Cingulate Cortex for Fibromyalgiafibromyalgia, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, rheumatic disorderRecruitingNot applicable2026-08-20NCT07226648
Metabolic and Hemodynamic Reserve in Pediatric SCACongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, brain disorder, central nervous system disorder, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, nervous system disorder, sickle cell diseaseActive, not recruitingNot applicable2026-08-19NCT04406818
PET Imaging With [18F]Fluselenamyl in People With Cardiac AmyloidosisAmyloid Neuropathies, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Immunoglobulin Light-chain Amyloidosis, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, amyloidosis, familial amyloid neuropathy, hereditary amyloidosis, hereditary disease, immune system disorder, immunoproliferative disorder, inborn errors of metabolism, inherited neurodegenerative disorder, lymphoproliferative syndrome, metabolic disease, monoclonal gammopathy, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, peripheral nervous system disorder, plasma cell neoplasm, proteostasis deficienciesEnrolling by invitationPhase 12026-08-18NCT07771621