A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort
Recruiting · NCT04626674 · Registry updated 2026-09-11Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Phase 1 | 2026-09-11 | NCT04626674 |
2 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Hoffmann-La Roche | 280 |
| Sarepta Therapeutics, Inc. | 15 |
12 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann & Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 144 |
| Arkansas Children's Hospital | Little Rock | United States | 82 |
| Children's Hospital of The King's Daughters | Norfolk | United States | 87 |
| Duke University Medical Center | Durham | United States | 52 |
| Nationwide Children's Hospital | Columbus | United States | 309 |
| Neurology Rare Disease Center | Flower Mound | United States | 8 |
| Stanford University | Palo Alto | United States | 161 |
| University of California, Davis | Sacramento | United States | 3 |
| University of California, Los Angeles | Los Angeles | United States | 142 |
| University of California, San Diego | La Jolla | United States | 25 |
| University of Florida | Gainesville | United States | 144 |
| Washington University in St. Louis | St Louis | United States | 79 |