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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-101 in Participants With Myotonic Dystrophy Type 1Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Disorders, Atrophic, hereditary disease, inherited neurodegenerative disorder, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, myotonic dystrophy, myotonic syndrome, nervous system disorder, neurodegenerative disease, neuromuscular diseaseActive, not recruitingPhase 1 / Phase 22026-09-23NCT05481879

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OrganizationsLinked trials
Dyne Therapeutics7

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Research sitesCityCountryLinked trials
Centro Clinico NemoMilanItaly3
Charité - Universitätsmedizin BerlinBerlinGermany28
Chu de NantesNantesFrance72
Fondazione Policlinico Universitario A Gemelli-RomeRomeItaly2
Indiana University School of MedicineIndianapolisUnited States71
Institut de MyologieParisFrance2
John Walton Muscular Dystrophy Research CentreNewcastle upon TyneUnited Kingdom1
Ludwig Maximilians University, Munich - Friedrich Baur InstitutMunichGermany1
Neurology Rare Disease CenterDentonUnited States6
NZCR AucklandAucklandNew Zealand1
Radboud Medical CenterNijmegenNetherlands1
Salford Royal HospitalSalfordUnited Kingdom25
St. Vincent's HospitalFitzroyAustralia5
Stanford UniversityStanfordUnited States213
University College London HospitalsLondonUnited Kingdom7
University of Florida College of MedicineGainesvilleUnited States14
University of IowaIowa CityUnited States284
University of Rochester Medical CenterRochesterUnited States162
Virginia Commonwealth University (VCU)RichmondUnited States4
Washington University in St. LouisSt LouisUnited States79