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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study About Antibody Levels and Biomarkers in the Blood in People With Late-onset Pompe DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderActive, not recruitingNot applicable2026-10-08NCT06150820
Boosting Resources for Tracheostomy Care at HomeCaregiver Burden; TracheostomyEnrolling by invitationNot applicable2026-09-30NCT06283953
Caloric Restriction and Activity to Reduce Chemoresistance in B-ALLB-cell acute lymphoblastic leukemia, B-cell neoplasm, Body Weight, Burkitt lymphoma, DNA Virus Infections, Epstein-Barr virus infection, Hemic and Lymphatic Diseases, Herpesviridae infectious disease, Infections, Leukemia, B-Cell, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Pediatric Obesity, Precursor Cell Lymphoblastic Leukemia-Lymphoma, Signs and Symptoms, Tumor Virus Infections, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, neoplasm, nutritional disorder, obesity disorder, overnutrition, viral infectious diseaseRecruitingPhase 22026-08-19NCT05082519
Streamlined Treatment of Pulmonary Exacerbations in PediatricsCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot applicable2026-08-03NCT06654752
Rethinking Early Airway Clearence TherapiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderNot yet recruitingNot applicable2026-07-10NCT07696338
Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young ChildrenCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-07-08NCT04509050