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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Study to Evaluate Biological & Clinical Effects of Significantly Corrected CFTR Function in Infants & Young ChildrenCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorderRecruitingNot stated2026-07-08NCT04509050

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Research sitesCityCountryLinked trials
Baylor College of MedicineHoustonUnited States306
Boston Children's HospitalBostonUnited States343
Children's Hospital ColoradoAuroraUnited States312
Children's Hospital of New YorkNew YorkUnited States4
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Children's Hospital of Pittsburgh of UPMCPittsburghUnited States120
Children's Hospitals and Clinics of MinnesotaMinneapolisUnited States6
Children's Mercy Kansas CityKansas CityUnited States17
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Cook Children's Medical CenterFort WorthUnited States111
Helen DeVos Children's HospitalGrand RapidsUnited States23
Hershey Medical Center Pennsylvania State UniversityHersheyUnited States4
Nationwide Children's HospitalColumbusUnited States309
Nemours Children's ClinicJacksonvilleUnited States7
New York Medical College at Westchester Medical CenterValhallaUnited States5
Oklahoma Cystic Fibrosis CenterOklahoma CityUnited States2
Oregon Health Sciences UniversityPortlandUnited States33
Primary Children's Cystic Fibrosis CenterSalt Lake CityUnited States2
Riley Hospital for ChildrenIndianapolisUnited States134
Seattle Children's HospitalSeattleUnited States281
St. Louis Children's HospitalSt LouisUnited States30
Stanford University Medical CenterPalo AltoUnited States28
SUNY Upstate Medical UniversitySyracuseUnited States68
The Children's Hospital Alabama, University of Alabama at BirminghamBirminghamUnited States5
The Cystic Fibrosis Center of Western New YorkBuffaloUnited States4