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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study About Antibody Levels and Biomarkers in the Blood in People With Late-onset Pompe DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorderActive, not recruitingNot applicable2026-10-08NCT06150820

1 results · Page 1 of 1

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OrganizationsLinked trials
Astellas Gene Therapies6

53 results · Page 1 of 3

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Research sitesCityCountryLinked trials
AU61001HerstonAustralia1
AU61003AdelaideAustralia1
BR55001São PauloBrazil1
BR55002Porto AlegreBrazil1
BR55003FlamengoBrazil1
CA15001MontrealCanada1
Children's Hospitals and Clinics of MinnesotaMinneapolisUnited States6
CN15003EdmontonCanada1
DT49003HöchheimGermany1
DT49004EssenGermany1
DT49005BonnGermany1
DT49006MünsterGermany1
Emory ClinicAtlantaUnited States12
ES34001MadridSpain1
ES34002ValenciaSpain1
ES34003AlbaceteSpain1
ES34004BarcelonaSpain1
ES34005MadridSpain1
ES34007L'Hospitalet de LlobregatSpain1
ES34009Donostia / San SebastianSpain1
FR33001StrasbourgFrance1
FR33002MarseilleFrance1
FR33003NantesFrance1
FR33004NiceFrance1
FR33005LilleFrance1