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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
ATTUNE: A Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of Intrathecally-Administered ION440 in Participants With Methyl CpG Binding Protein 2 (MECP2) Duplication Syndrome (MDS)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Rett syndrome, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorderRecruitingPhase 1 / Phase 22026-10-08NCT06430385
A Prospective Analysis of Long-Term Clinical Outcomes and 3D Spine Growth in Anterior Vertebral Body TetheringScoliosis IdiopathicRecruitingNot applicable2026-09-28NCT04914507
Chronic Postsurgical PainBrain Damage, Chronic, Chronic Pain, Chronic Postoperative Pain, Neurologic Manifestations, Pain, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Postoperative Complications, Postoperative Pain, Signs and Symptoms, brain disorder, central nervous system disorder, cerebral palsy, nervous system disorderRecruitingNot stated2026-09-25NCT05764681
Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of ApitegromabAtrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Atrophy, Spinal, Type II, Neurologic Manifestations, Neuromuscular Manifestations, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Spinal Muscular Atrophies of Childhood, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, muscular atrophy, nervous system disorder, neurodegenerative disease, neuromuscular disease, proximal spinal muscular atrophy, spinal cord disorder, spinal muscular atrophy, spinal muscular atrophy, type IIIActive, not recruitingPhase 32026-09-01NCT05626855
Distal Radius Interventions for Fracture TreatmentArm Injuries, Wrist Fractures, Wrist Injuries, bone fracture, injuryRecruitingNot applicable2026-07-01NCT05131685
Rett Syndrome RegistryCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Rett Syndrome, Atypical, Rett syndrome, Signs and Symptoms, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorderRecruitingNot stated2026-06-30NCT05432349
Establishing the Preliminary Utility of a Novel Pediatric Manual Mobile Standing WheelchairCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, central nervous system malformation, nervous system disorder, spina bifidaRecruitingNot applicable2026-06-24NCT07290556
Casting vs Bracing for Idiopathic Early-Onset ScoliosisEarly-Onset Scoliosis Deformity of Spine; Scoliosis IdiopathicActive, not recruitingNot applicable2026-03-13NCT04500041
Safety and Efficacy of TSHA-102 in Pediatric Females With Rett Syndrome (REVEAL Pediatric Study)Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neurobehavioral Manifestations, Neurologic Manifestations, Rett syndrome, X-linked disease, hereditary disease, inherited neurodegenerative disorder, intellectual disability, nervous system disorder, neurodevelopmental disorder, psychiatric disorderActive, not recruitingPhase 1 / Phase 22025-10-15NCT06152237
Multicenter Prospective Cohort Study on Current Treatments of Legg-Calvé-Perthes DiseaseLegg-Calve-Perthes disease, Necrosis, Pathologic Processes, Pathological Conditions, Signs and Symptoms, bone disorder, familial avascular necrosis of femoral head, musculoskeletal system disorder, osteonecrosisEnrolling by invitationNot stated2025-05-06NCT02040714
Virtual Reality During Pediatric Cast Removalbone fracture, injuryRecruitingNot applicable2021-02-11NCT03903510