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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Long-Term Safety & Efficacy of Apitegromab in Patients With SMA Who Completed Previous Trials of ApitegromabAtrophy, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Muscular Atrophy, Spinal, Type II, Neurologic Manifestations, Neuromuscular Manifestations, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Spinal Muscular Atrophies of Childhood, central nervous system disorder, hereditary disease, inherited neurodegenerative disorder, motor neuron disorder, muscular atrophy, nervous system disorder, neurodegenerative disease, neuromuscular disease, proximal spinal muscular atrophy, spinal cord disorder, spinal muscular atrophy, spinal muscular atrophy, type IIIActive, not recruitingPhase 32026-09-01NCT05626855

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OrganizationsLinked trials
Scholar Rock, Inc.4

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Research sitesCityCountryLinked trials
Boston Children's HospitalBostonUnited States343
Carlo Besta Neurological Research InstituteMilanItaly1
Children's Hospital ColoradoAuroraUnited States312
Children's Hospital Los AngelesLos AngelesUnited States226
Children's Specialty Group PLLC (Children's Hospital of The King's Daughters)Newport NewsUnited States1
CHR CitadelleLiègeBelgium5
CHRU de Lille - Hpital Jeanne de FlandreLilleFrance1
CHU Toulouse Hopital des EnfantsToulouseFrance2
Columbia University Medical centerNew YorkUnited States224
Fondazione Policlinico Universitario A. GemelliRomaItaly1
Gillette Children's Specialty HealthcareSaint PaulUnited States11
Great Ormond Street Hospital For ChildrenLondonUnited Kingdom2
Helen DeVos Children's HospitalGrand RapidsUnited States23
Hopital Trousseau - I-MotionParisFrance2
Hospital Sant Joan de DeauBarcelonaSpain1
Hospital Universitari i Politecnic La FeValenciaSpain93
Instytut Pomnik - Centrum Zdrowia DzieckaWarsawPoland3
Istituto Giannina Gaslini, Centro Traslazionale di Miologia e Patologie NeurodegenerativeGenovaItaly1
Johns Hopkins HospitalBaltimoreUnited States135
Klinikum der Universitat Munchen, Dr. von Haunersches Kinderspital, Abteilung fur Kinderneurologie und EntwicklungsneurologieMunchen, BayernGermany1
Leeds Children's Hospital Clinical ResearchLeedsUnited Kingdom1
Lurie Children's Hospital of ChicagoChicagoUnited States16
Nationwide Children's HospitalColumbusUnited States12
Nemours Biomedical ResearchOrlandoUnited States1
NeuroMuscular OmnicentreMilanItaly1