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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Post-Approval Study of PALMAZ MULLINS XD™ in Treating Pulmonary Artery StenosisArterial Occlusive Diseases, Stenosis, Pulmonary Artery, cardiovascular disorder, vascular disorderRecruitingNot stated2026-10-02NCT07122518
Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorderRecruitingPhase 1 / Phase 22026-09-24NCT06270316
Safety Study to Evaluate the Occurrence of EFAD in Pediatric Patients With PNAC Who Require More Than Eight Weeks of Omegaven TreatmentHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Nutritional and Metabolic Diseases, Precursor Cell Lymphoblastic Leukemia-Lymphoma, childhood acute lymphoblastic leukemia, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasm, nutritional deficiency disease, nutritional disorderRecruitingNot stated2026-08-14NCT06274788
Biliary Atresia Study in Infants and ChildrenCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, bile duct disorder, biliary atresia, biliary tract disorder, cholestasisRecruitingNot stated2026-06-04NCT00345553
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical PracticeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseEnrolling by invitationNot stated2025-09-10NCT06606340