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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical PracticeCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseEnrolling by invitationNot stated2025-09-10NCT06606340

1 results · Page 1 of 1

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OrganizationsLinked trials
Sarepta Therapeutics, Inc.15

20 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Arkansas Children's Hospital Research InstituteLittle RockUnited States6
Atrium Health Wake Forest University Health SciencesWinston-SalemUnited States1
Children's Hospital Los AngelesLos AngelesUnited States226
Children's Hospital Medical CenterCincinnatiUnited States5
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Children's National HospitalWashington D.C.United States100
Columbia University Medical Center - PINNew YorkUnited States1
Cook Children's HospitalFort WorthUnited States6
Duke Lenox Baker Children's HospitalDurhamUnited States1
Kennedy Krieger InstituteBaltimoreUnited States3
Nationwide Children's HospitalColumbusUnited States309
Penn State Health Milton S. Hershey Medical CenterHersheyUnited States1
Seattle Children's HospitalSeattleUnited States281
Texas Children's HospitalHoustonUnited States187
University of California Davis Medical CenterSacramentoUnited States29
University of FloridaGainesvilleUnited States144
University of Iowa Hospitals and ClinicsIowa CityUnited States99
UPMC Children's Hospital of PittsburghPittsburghUnited States6
UVA Children's HospitalCharlottesvilleUnited States2
Washington UniversitySt LouisUnited States182