Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease | ClinicalTrials HQ

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease	Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder	Recruiting	Phase 1 / Phase 2	2026-09-24		NCT06270316

1 results · Page 1 of 1

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Organizations	Linked trials
UniQure Biopharma B.V.	5

10 results · Page 1 of 1

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Research sites	City	Country	Linked trials
Ann & Robert H. Lurie Children's Hospital of Chicago	Chicago	United States	144
Children's Hospital Medical Center	Cincinnati	United States	5
Emory University School of Medicine	Atlanta	United States	47
Lysosomal & Rare Disorders Research and Treatment Center, Inc	Fairfax	United States	1
MHealth Fairview University of Minnesota Medical Center East Bank	Minneapolis	United States	1
NYC Health + Hospitals/Metropolitan	New York	United States	1
The Kirklin Clinic of University of Alabama Birmingham Hospital	Birmingham	United States	3
University of California Los Angeles (UCLA)	Los Angeles	United States	11
University of Utah, Clinical and Translational Sciences Institute	Salt Lake City	United States	3
UPMC Children's Hospital of Pittsburgh	Pittsburgh	United States	70