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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Pegtibatinase as a Treatment for Participants With Classical Homocystinuria (HCU) Receiving Standard of Care TreatmentBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorderRecruitingPhase 32026-10-08NCT06247085
An Open-label Extension Study to Evaluate Long-term Efficacy and Safety of Odevixibat in Children With Biliary AtresiaCongenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, bile duct disorder, biliary atresia, biliary tract disorderActive, not recruitingPhase 32026-10-01NCT05426733
A Long-term Safety and Efficacy Study of N-Acetyl-GED-0507-34-LEVO Gel 5%, in Subjects With Acne Vulgaris (GEDACNE-LT)Acneiform Eruptions, Skin and Connective Tissue Diseases, acne, sebaceous gland disorder, skin disorderActive, not recruitingPhase 32026-09-15NCT07389109
The CROCO Study: CROhn's Disease COhort StudyCrohn disease, Digestive System Diseases, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorderActive, not recruitingNot applicable2026-07-28NCT05420233
Harmony TPV EMEA PMScardiovascular disorder, heart disorder, heart valve disorder, pulmonary valve insufficiencyRecruitingNot applicable2026-07-14NCT06906926
Tepotinib Phase II in NSCLC Harboring MET Alterations (VISION)Neoplasms by Histologic Type, Neoplasms by Site, Thoracic Neoplasms, adenocarcinoma, bronchial neoplasm, bronchogenic carcinoma, carcinoma, epithelial neoplasm, lung disorder, lung neoplasm, neoplasm, non-small cell lung carcinoma, respiratory system disorder, respiratory tract neoplasmActive, not recruitingPhase 22026-07-14NCT02864992
A Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, brain disorder, central nervous system disorder, connective tissue disorder, hereditary disease, homocystinuria, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorderEnrolling by invitationPhase 32026-05-28NCT06431893
A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingNot stated2026-03-25NCT05813678
Efficacy and Safety of XyloCore Peritoneal Dialysis Solution.Chronic Disease, Disease Attributes, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Urogenital Diseases, chronic renal failure syndrome, kidney disorder, kidney failure, urinary system disorderRecruitingPhase 32026-03-24NCT03994471
CACP: Study on Camptodactyly - Arthropathy - Coxa Vara - Pericarditis (CACP) SyndromeBone Anteversion, Bone Malalignment, Pathologic Processes, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Torsion Abnormality, arthropathy, bone disorder, cardiovascular disorder, coxa vara, disease, heart disorder, musculoskeletal system disorder, pericarditis, syndromic diseaseRecruitingNot stated2026-03-16NCT07468461
Observational Study on Skeletal Ewing's SarcomaEwing sarcoma, Ewing sarcoma of bone, Neoplasms by Histologic Type, Neoplasms, Bone Tissue, Neoplasms, Connective and Soft Tissue, connective tissue neoplasm, neoplasm, osteosarcoma, sarcomaRecruitingNot stated2026-01-02NCT04845893
Phase II Study of Radiotherapy Followed by Durvalumab and Ceralasertib in Stage III NSCLC Patients With Thoracic Relapses +/- Oligometastases After PACIFIC RegimenNon Small Cell Lung Cancer NSCLCRecruitingPhase 22025-12-18NCT06680050
Loop Diuretic Therapy in Acutely Decompensated Heart FailureFemale Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Male Urogenital Diseases, Urogenital Diseases, cardiovascular disorder, heart disorder, heart failure, kidney disorder, kidney failure, urinary system disorderRecruitingNot stated2025-08-08NCT02638142
Treatment Protocol for Children and Adolescents With Acute Lymphoblastic Leukemia - AIEOP-BFM ALL 2017Hemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoproliferative syndrome, neoplasmRecruitingPhase 32025-04-06NCT03643276
National Database on Primary Sclerosing Cholangitis (PSC)Cholangitis, Sclerosing, Digestive System Diseases, bile duct disorder, biliary tract disorder, cholangitis, primary sclerosing cholangitisRecruitingNot stated2024-01-02NCT05618145