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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace)Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuriaRecruitingNot stated2026-03-25NCT05813678

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OrganizationsLinked trials
BioMarin Pharmaceutical32

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