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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
NIAID Centralized Sequencing ProtocolCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Primary Immunodeficiency Diseases, autoimmune disease, hereditary disease, immune system disorder, inborn error of immunityRecruitingNot stated2026-10-02NCT03206099
Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMITCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-09-24NCT06564974
Hospital-Based Cluster Trial: Magnetically Controlled Growing Rods Using Distraction IntervalsEarly-Onset Scoliosis Deformity of SpineActive, not recruitingNot applicable2026-09-24NCT04058561
Study of Bictegravir/Emtricitabine/Tenofovir Alafenamide Fixed Dose Combination in Adolescents and Children With Human Immunodeficiency Virus-1HIV-1 InfectionActive, not recruitingPhase 2 / Phase 32026-09-24NCT02881320
Mucopolysaccharidosis VII Disease Monitoring ProgramCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, Skin and Connective Tissue Diseases, connective tissue disorder, cutaneous mucinosis, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, mucopolysaccharidosis, mucopolysaccharidosis type 7RecruitingNot stated2026-08-27NCT03604835
Adoptive Cord Blood Immunotherapy for EBV, CMV, BKV and Adenovirus Reactivation/Infection or ProphylaxisInfections, viral infectious diseaseActive, not recruitingPhase 1 / Phase 22026-08-14NCT03594981
Development of a Therapeutic Endpoint in Pediatric Rheumatologic ConditionsSkin and Connective Tissue Diseases, arthritic joint disease, arthropathy, autoimmune disease, connective tissue disorder, fibromyalgia, immune system disorder, juvenile idiopathic arthritis, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular disease, rheumatic disorder, systemic lupus erythematosusRecruitingNot stated2026-07-24NCT04833465
Physiologic Measure of VIPNChemotherapy-induced Peripheral NeuropathyRecruitingNot stated2026-07-24NCT04786977
A Study to Assess Growth in Children With Idiopathic Short StatureIdiopathic Short StatureRecruitingNot stated2026-06-23NCT06309979
Mesenchymal Stromal Cells for Infants With Congenital Heart Disease (MedCaP)Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderActive, not recruitingPhase 12026-06-02NCT04236479
Pilot Imaging Study of LeukemiaHemic and Lymphatic Diseases, Neoplasms by Histologic Type, Precursor Cell Lymphoblastic Leukemia-Lymphoma, acute myeloid leukemia, hematologic disorder, immune system disorder, immunoproliferative disorder, leukemia, lymphatic system disorder, lymphoid leukemia, lymphoma, lymphoproliferative syndrome, myeloid leukemia, neoplasm, plasma cell neoplasmRecruitingPhase 12026-04-23NCT03633955
Therapeutic Endpoint in Pediatric IBD ConditionsCrohn disease, Digestive System Diseases, colitis, colonic disorder, digestive system disorder, gastroenteritis, inflammatory bowel disease, intestinal disorder, ulcerative colitisRecruitingNot stated2026-04-08NCT06065228
Measuring Analgesic InterventionsNeurobehavioral Manifestations, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, agnosia, nervous system disorder, perceptual disordersRecruitingNot stated2026-04-07NCT03794362
Developing a Method to Objectively Measure Opioid AnalgesiaNeurobehavioral Manifestations, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, agnosia, nervous system disorder, perceptual disordersActive, not recruitingNot stated2026-04-06NCT03605966
Minimizing Toxicity in HLA-identical Sibling Donor Transplantation for Children With Sickle Cell DiseaseCongenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, sickle cell diseaseRecruitingPhase 22026-03-10NCT03587272
The Pediatric Anesthesia Quality Improvement ProjectAnesthesia; Children; SurgeryRecruitingNot stated2025-05-21NCT00674388
A Multicenter Multinational Observational Study of Children With HypochondroplasiahypochondroplasiaRecruitingNot stated2025-04-03NCT06212947
Technical Development for Pediatric Cardiovascular MRICardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorderActive, not recruitingNot stated2022-04-14NCT02892136
Whole Body MRI to Identify Atypical Neurofibromas in Patients With NF1Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Neoplasms by Histologic Type, Neoplasms, Nerve Tissue, atypical neurofibroma, hereditary disease, hereditary neoplastic syndrome, inherited neurodegenerative disorder, neoplasm, nerve sheath neoplasm, nervous system disorder, neurocutaneous syndrome, neurodegenerative disease, neurofibroma, neurofibromatosis, neurofibromatosis type 1, neurofibromatosis, type IV, of Riccardi, neuromuscular disease, peripheral nervous system disorder, peripheral nervous system neoplasm, plexiform neurofibromaActive, not recruitingNot applicable2021-03-02NCT03820778