Shanghai Children's Medical Center
Shanghai Children's Medical Center
Shanghai, Shanghai Municipality, China4 results · Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Safety and Dystrophin Expression of SPOT-03 in Duchenne Muscular Dystrophy (DMD) Patients | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Duchenne muscular dystrophy, Muscular Disorders, Atrophic, X-linked disease, hereditary disease, muscle tissue disorder, muscular dystrophy, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Early phase 1 | 2026-05-07 | NCT07188012 | |
| Evaluate the Safety and Preliminary Efficacy of EXG110 in Subjects With Fabry Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Not applicable | 2026-02-27 | NCT06539624 | |
| CS-121 APOC3 Base Editing in Children and Adolescents With Hyperchylomicronemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Dyslipidemias, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Nutritional and Metabolic Diseases, familial lipoprotein lipase deficiency, hereditary disease, hyperlipidemia, hyperlipoproteinemia, inborn errors of metabolism, metabolic disease, pancreas disorder, pancreatitis | Recruiting | Early phase 1 | 2026-01-28 | NCT07371767 | |
| A First-ever Research Collaboration to Characterize MRI Measured Neural Flexibility Development in Chinese Toddlers | Brain; Growth & Development | Recruiting | Not stated | 2025-12-03 | NCT04916652 |