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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Evaluate the Safety and Preliminary Efficacy of EXG110 in Subjects With Fabry DiseaseBrain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorderRecruitingNot applicable2026-02-27NCT06539624

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Research sitesCityCountryLinked trials
Children's Hospital, Zhejiang University School of MedicineHangzhouChina8
Shanghai Children's Medical CenterShanghaiChina4