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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
Evaluation of Outcome Metrics in Alexander DiseaseAlexander disease, Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hereditary Central Nervous System Demyelinating Diseases, Leukoencephalopathies, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, demyelinating disease, hereditary disease, inborn errors of metabolism, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative diseaseRecruitingNot stated2026-01-15NCT02714764

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Research sitesCityCountryLinked trials
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434