Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria
Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria
Active, not recruiting · NCT05270837 · Registry updated 2026-07-21Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Active, not recruiting | Phase 3 | 2026-07-21 | NCT05270837 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| BioMarin Pharmaceutical | 32 |
16 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Ann and Robert H. Lurie Children's Hospital of Chicago | Chicago | United States | 14 |
| Arkansas Children's Hospital | Little Rock | United States | 82 |
| Boston Children's Hospital | Boston | United States | 343 |
| Charité - Universitätsmedizin Berlin | Berlin | Germany | 21 |
| Children's Hospital of Colorado | Aurora | United States | 28 |
| Children's Hospital of Wisconsin | Milwaukee | United States | 87 |
| IU Health University Hospital | Indianapolis | United States | 15 |
| McGovern Medical School, University of Texas Health Science Center at Houston (UTHealth) | Houston | United States | 1 |
| Phoenix Children's Hospital | Phoenix | United States | 95 |
| Universitat Mainz | Mainz | Germany | 1 |
| University of Kentucky College of Medicine | Lexington | United States | 3 |
| University of Pittsburgh Medical Center | Pittsburgh | United States | 18 |
| University of South Florida | Tampa | United States | 65 |
| University of Utah Medical Center | Salt Lake City | United States | 5 |
| University of Virginia School of Medicine | Charlottesville | United States | 6 |
| Universitätsklinikum Hamburg-Eppendorf | Hamburg | Germany | 31 |