University of Pittsburgh Medical Center
University of Pittsburgh Medical Center
Pittsburgh, Pennsylvania, United States18 results ยท Page 1 of 1
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Phase 2 Study to Assess the Safety and Efficacy of ANG003 | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, exocrine pancreatic insufficiency, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Recruiting | Phase 2 | 2026-10-06 | NCT07450547 | |
| Bowel Continence Across the Lifespan in People With Spina Bifida | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Fecal Incontinence, central nervous system malformation, colonic disorder, digestive system disorder, functional colonic disease, intestinal disorder, nervous system disorder, neurogenic bowel, rectal disorder, spina bifida | Recruiting | Not stated | 2026-09-24 | NCT07390318 | |
| Liver Transplantation From Donors With HIV: Impact on Opportunistic Infections, Cancer, and Long-Term Outcomes (Expanding HOPE Liver) | HIV | Recruiting | Not applicable | 2026-09-09 | NCT07665372 | |
| Coupled Gentamicin-Lactobacillus Rhamnosus in NLUTD | CNS demyelinating autoimmune disease, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Female Urogenital Diseases, Female Urogenital Diseases and Pregnancy Complications, Infections, Male Urogenital Diseases, Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Urinary Bladder, Neurogenic, Urogenital Diseases, autoimmune disease, autoimmune disorder of the nervous system, central nervous system disorder, central nervous system malformation, demyelinating disease, immune system disorder, injury, multiple sclerosis, nervous system disorder, nervous system injury, spina bifida, spinal cord disorder, spinal cord injury, urinary bladder disorder, urinary system disorder, urinary tract infection | Not yet recruiting | Early phase 1 | 2026-08-21 | NCT07643974 | |
| AAV Gene Therapy Clinical Study in Adult Classic PKU (PHEdom) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Recruiting | Phase 1 / Phase 2 | 2026-08-18 | NCT06332807 | |
| A Study of Nipocalimab in Children Aged 2 to Less Than 18 Years With Generalized Myasthenia Gravis | Neoplasms by Site, Paraneoplastic Syndromes, Nervous System, autoimmune disease, autoimmune disorder of the nervous system, immune system disorder, myasthenia gravis, neoplasm, nervous system disorder, neurodegenerative disease, neuromuscular disease, neuromuscular junction disease, paraneoplastic syndrome | Recruiting | Phase 2 / Phase 3 | 2026-07-31 | NCT05265273 | |
| Study to Evaluate the Safety and Efficacy of Pegvaliase in Adolescents (Ages 12-17) With Phenylketonuria | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Active, not recruiting | Phase 3 | 2026-07-21 | NCT05270837 | |
| Study to Enable New Diagnostics for Pulmonary Microbes in People With CF | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Recruiting | Not stated | 2026-07-02 | NCT07312734 | |
| A Long-term, Post-marketing Safety Study of Palynziq in Patients With PKU (PALace) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Recruiting | Not stated | 2026-03-25 | NCT05813678 | |
| Strength and Muscle Related Outcomes for Nutrition and Lung Function in CF | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Active, not recruiting | Not stated | 2026-03-13 | NCT05639556 | |
| Effect of Raised End-Tidal pCo2 on Choroidal Volume | Intraocular Pressure | Recruiting | Not applicable | 2026-01-09 | NCT06275308 | |
| Restarting Triple Therapy With Robust Monitoring for Adverse Events (RETRIAL) | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Recruiting | Not stated | 2025-11-03 | NCT06683092 | |
| Prospective Study of Pregnancy in Women With Cystic Fibrosis | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Active, not recruiting | Not stated | 2025-11-03 | NCT04828382 | |
| A Research Study to Advance the CF Therapeutics Pipeline for People Without Modulators | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Recruiting | Not stated | 2025-10-01 | NCT06504589 | |
| IV Gallium Study for Patients With Cystic Fibrosis Who Have NTM (ABATE Study) | Actinomycetales infectious disease, Bacterial Infections and Mycoses, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, Infections, Mycobacterium Infections, Nontuberculous, Mycobacterium avium complex disease, bacterial infectious disease, cystic fibrosis, gram-positive bacterial infections, hereditary disease, lung disorder, mycobacterial infectious disease, pancreas disorder, respiratory system disorder | Recruiting | Phase 1 | 2025-10-01 | NCT04294043 | |
| Strategy to Avoid Excessive Oxygen in Major Burn Patients | Critical Illness, Disease Attributes, Hyperoxia, Hypoxia, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Respiratory, burn, injury | Active, not recruiting | Phase 3 | 2025-04-02 | NCT04534972 | |
| Strategy to Avoid Excessive Oxygen for Critically Ill Trauma Patients | Critical Illness, Disease Attributes, Hyperoxia, Hypoxia, Pathologic Processes, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Signs and Symptoms, Respiratory, burn, injury | Active, not recruiting | Phase 3 | 2025-04-02 | NCT04534959 | |
| Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA) | central nervous system disorder, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, spinal cord disorder, spinal muscular atrophy | Recruiting | Not stated | 2025-01-31 | NCT04174157 |