Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia | ClinicalTrials HQ

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
Phase IA and IB Study of AAVrh.10hFXN Gene Therapy for the Cardiomyopathy of Friedreich's Ataxia	Cardiac Hypertrophy, Cardiomegaly, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Dyskinesias, Friedreich ataxia, Hypertrophy, Neurologic Manifestations, Nutritional and Metabolic Diseases, Pathological Conditions, Anatomical, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Spinocerebellar Degenerations, atactic disorder, non-human animal, brain disorder, cardiomyopathy, cardiovascular disorder, central nervous system disorder, cerebellar disorder, heart disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorder	Recruiting	Phase 1	2026-09-28		NCT05302271

2 results · Page 1 of 1

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Organizations	Linked trials
National Heart, Lung, and Blood Institute (NHLBI)	791
Weill Medical College of Cornell University	276

1 results · Page 1 of 1

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Research sites	City	Country	Linked trials
Weill Cornell Medicine	New York	United States	66