A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia | ClinicalTrials HQ

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Trial	Conditions	Status	Phase	Updated	More info	NCT ID
A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia	Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Friedreich ataxia, Nutritional and Metabolic Diseases, Spinocerebellar Degenerations, brain disorder, central nervous system disorder, cerebellar disorder, hereditary disease, inborn mitochondrial metabolism disorder, inherited neurodegenerative disorder, metabolic disease, nervous system disorder, neurodegenerative disease, spinal cord disorder	Active, not recruiting	Phase 3	2025-10-30		NCT05515536

1 results · Page 1 of 1

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Organizations	Linked trials
PTC Therapeutics	8

14 results · Page 1 of 1

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Research sites	City	Country	Linked trials
CBR Neurogenetic Research Clinic, University of Auckland	Auckland	New Zealand	1
Centre de Recherche du Centre Hospitalier de l'Université de Montreal (CRCHUM)	Montreal	Canada	1
CHU Sainte-Justine	Montreal	Canada	4
Department of Neurology and Hertie-Institute for Clinical Brain Research German Center of Neurodegenerative Diseases (DZNE)	Tübingen	Germany	1
Hospital Sant Joan de Déu Barcelona Unidad de Enfermedades Neuromusculares	Barcelona	Spain	1
Hôpital Pitié-Salpêtrière, Institut du Cerveau (Paris Brain Institute)	Paris	France	1
Murdoch Children's Research Institute	Parkville	Australia	21
Ospedale Pediatrico Bambino Gesu' IRCCS	Roma	Italy	1
The Children's Hospital of Philadelphia	Philadelphia	United States	62
UCLA	Los Angeles	United States	80
University of Campinas (UNICAMP) - School of Medical Sciences, Dept of Neurology	São Paulo	Brazil	1
University of Florida	Gainesville	United States	70
University of Iowa	Iowa City	United States	284
University of South Florida	Tampa	United States	73