4D-310 in Adults With Fabry Disease and Cardiac Involvement
4D-310 in Adults With Fabry Disease and Cardiac Involvement
Recruiting · NCT05629559 · Registry updated 2025-02-21Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| 4D-310 in Adults With Fabry Disease and Cardiac Involvement | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Phase 1 / Phase 2 | 2025-02-21 | NCT05629559 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| 4D Molecular Therapeutics | 10 |
4 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Royal Melbourne Hospital | Melbourne | Australia | 3 |
| Royal Perth Hospital | Perth | Australia | 12 |
| Taipei Veterans General Hospital | Taipei | Taiwan | 189 |
| Westmead Hospital | Westmead | Australia | 23 |