Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)
Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS)
Active, not recruiting · NCT06100276 · Registry updated 2025-10-22Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| Safety, Tolerability, and Exploratory Efficacy Study of Intrathecally Administered Gene Therapy AMT-162 in Adult Participants With SOD1 Amyotrophic Lateral Sclerosis (SOD1-ALS) | Nutritional and Metabolic Diseases, TDP-43 proteinopathy, amyotrophic lateral sclerosis, central nervous system disorder, metabolic disease, motor neuron disorder, nervous system disorder, neurodegenerative disease, neuromuscular disease, proteostasis deficiencies, spinal cord disorder | Active, not recruiting | Phase 1 / Phase 2 | 2025-10-22 | NCT06100276 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| UniQure Biopharma B.V. | 5 |
12 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Barrow Neurological Institute | Phoenix | United States | 50 |
| California Pacific Medical Center | San Francisco | United States | 9 |
| Columbia University Irving Medical Center | New York | United States | 234 |
| Massachusetts General Hospital, Sean M. Healey and AMG Center for ALS Research | Boston | United States | 1 |
| Mayo Clinic Florida | Jacksonville | United States | 105 |
| Mayo Clinic Rochester | Rochester | United States | 133 |
| Norrlands Universitetssjukhus | Umeå | Sweden | 1 |
| Northwestern University Feinberg School Of Medicine | Chicago | United States | 49 |
| University of California Irvine | Irvine | United States | 30 |
| University of Kansas Medical Center | Fairway | United States | 18 |
| University of Pennsylvania School of medicine | Philadelphia | United States | 6 |
| Winship Cancer Institute of Emory University | Atlanta | United States | 45 |