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TrialConditionsStatusPhaseUpdatedMore infoNCT ID
A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Conditioncongenital structural myopathy, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular diseaseRecruitingNot stated2026-09-30NCT06581146

1 results · Page 1 of 1

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OrganizationsLinked trials
Astellas Gene Therapies6

11 results · Page 1 of 1

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Research sitesCityCountryLinked trials
Ann & Robert H. Lurie Children's Hospital of ChicagoChicagoUnited States144
Boston Children's HospitalBostonUnited States343
Children's Hospital of PhiladelphiaPhiladelphiaUnited States434
Cincinnati Children's Hospital Medical CenterCincinnatiUnited States405
Site CA15001TorontoCanada1
Site GB44003LondonUnited Kingdom2
Site GB44005OxfordUnited Kingdom1
Site GB44006LeedsUnited Kingdom1
UCLA Neurological ServicesSanta MonicaUnited States1
University of UtahSalt Lake CityUnited States137
UPMC Children's Hospital of PittsburghPittsburghUnited States70