UPMC Children's Hospital of Pittsburgh
UPMC Children's Hospital of Pittsburgh
Pittsburgh, Pennsylvania, United States70 results · Page 1 of 3
Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study Evaluating the Long-term Safety and Efficacy of VX-121 Combination Therapy | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, Infant, Newborn, Diseases, cystic fibrosis, hereditary disease, lung disorder, pancreas disorder, respiratory system disorder | Active, not recruiting | Phase 3 | 2026-10-09 | NCT05444257 | |
| Peer Support for Adolescents and Emerging Adults With Sickle Cell Pain | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Hemic and Lymphatic Diseases, Neurobehavioral Manifestations, Neurologic Manifestations, Pain, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, agnosia, anemia, familial hemolytic anemia, hematologic disorder, hemolytic anemia, hereditary disease, inherited hemoglobinopathy, nervous system disorder, perceptual disorders, sickle cell disease | Recruiting | Not applicable | 2026-10-08 | NCT06374238 | |
| Clinical and Laboratory Study of Methylmalonic Acidemia | Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, hereditary disease, hyperhomocysteinemia, inborn disorder of amino acid metabolism, inborn errors of metabolism, inborn organic aciduria, malabsorption syndrome, metabolic disease, methylmalonic acidemia, nutritional deficiency disease, nutritional disorder, vitamin B deficiency, vitamin deficiency disorder | Recruiting | Not stated | 2026-10-08 | NCT00078078 | |
| A Multicenter Study to Assess the Feasibility of 5-Aminolevulinic Acid (5-ALA) in Pediatric Brain Tumor Patients | Neoplasms by Site, brain disorder, central nervous system cancer, central nervous system disorder, neoplasm, nervous system disorder | Not yet recruiting | Phase 2 | 2026-10-07 | NCT06907485 | |
| A Platform Trial for Pediatric Participants With Obesity or Overweight (LY900040) | Body Weight, Nutritional and Metabolic Diseases, Overweight, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, nutritional disorder, obesity disorder, overnutrition | Recruiting | Phase 3 | 2026-10-07 | NCT06672549 | |
| Real-time Engagement for Learning to Effectively Control Type 2 Diabetes | Nutritional and Metabolic Diseases, diabetes mellitus, endocrine system disorder, glucose metabolism disease, hyperglycemia, metabolic disease, type 2 diabetes mellitus | Recruiting | Not applicable | 2026-10-07 | NCT06375460 | |
| ALTERRA Post-Approval Study | Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, heart valve disorder, pulmonary valve insufficiency, tetralogy of fallot | Active, not recruiting | Not stated | 2026-10-05 | NCT05378386 | |
| Harmony TPV Post-Approval Study | Cardiovascular Abnormalities, Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, cardiovascular disorder, congenital heart disease, heart disorder, heart valve disorder, pulmonary valve insufficiency, tetralogy of fallot | Active, not recruiting | Not applicable | 2026-10-01 | NCT05077774 | |
| A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition | congenital structural myopathy, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder, neuromuscular disease | Recruiting | Not stated | 2026-09-30 | NCT06581146 | |
| A Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of AG-181 in Subjects With Phenylketonuria | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn disorder of amino acid metabolism, inborn errors of metabolism, metabolic disease, nervous system disorder, phenylketonuria | Recruiting | Phase 1 | 2026-09-28 | NCT07241234 | |
| Safety, PK/PD, and Exploratory Efficacy Study of AMT-191 in Classic Fabry Disease | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Phase 1 / Phase 2 | 2026-09-24 | NCT06270316 | |
| High vs.Standard Dose Influenza Vaccine in Pediatric Solid Organ Transplant (SOT) Recipients | Disease Attributes, Infections, Pathologic Processes, Pathological Conditions, Signs and Symptoms, RNA Virus Infections, infectious disease, influenza, respiratory system disorder, respiratory tract infectious disorder, viral infectious disease | Recruiting | Phase 2 | 2026-09-24 | NCT05947071 | |
| A Phase I/II Trial of JR-446 in Mucopolysaccharidosis Type IIIB (MPS IIIB) | Mucopolysaccharidosis IIIB | Recruiting | Phase 1 / Phase 2 | 2026-09-21 | NCT07640984 | |
| Ketamine add-on Therapy for Established Status Epilepticus Treatment Trial (KESETT) | Neurologic Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, Status Epilepticus, nervous system disorder, visual epilepsy | Recruiting | Phase 3 | 2026-09-17 | NCT06907173 | |
| ZIP Study-OL Study of Safety, PK, Efficacy, PD, Immunogenicity of ATB200/AT2221 in Pediatrics Aged 0 to < 18 y.o. w/LOPD | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, disorder of glycogen metabolism, glycogen storage disease II, hereditary disease, inborn carbohydrate metabolic disorder, inborn errors of metabolism, lysosomal storage disease, metabolic disease, nervous system disorder | Active, not recruiting | Phase 3 | 2026-09-17 | NCT03911505 | |
| I-DECIDE After Bronchiolitis Hospitalization | Bronchiolitis Acute | Recruiting | Not applicable | 2026-09-10 | NCT07243652 | |
| A Study of Patients With Fabry Disease (US Specific) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Not stated | 2026-09-09 | NCT06906367 | |
| The PRISM-Social Needs (PRISM-SN) Intervention for Adolescents and Young Adults With Cancer | cancer, neoplasm | Active, not recruiting | Not applicable | 2026-09-09 | NCT06242964 | |
| A Gaucher Disease Gene Therapy Trial With FLT201 | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Gaucher Disease, Type 1, Gaucher disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, brain disorder, central nervous system disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis | Recruiting | Phase 3 | 2026-09-03 | NCT07223944 | |
| A Study of Migalastat in Pediatric Subjects (2 to <12 Yrs) With Fabry Disease and Amenable GLA Variants | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Phase 3 | 2026-09-01 | NCT06904261 | |
| SAFety and Efficacy of Human Anti-thymocyte ImmunoGlobUlin SAB-142 ARresting Progression of Type 1 Diabetes | Nutritional and Metabolic Diseases, autoimmune disease, diabetes mellitus, endocrine system disorder, glucose metabolism disease, immune system disorder, metabolic disease, type 1 diabetes mellitus | Recruiting | Phase 2 | 2026-08-24 | NCT07187531 | |
| A-LiNK: Improving Outcomes in Autoimmune Liver Disease | Cholangitis, Sclerosing, Digestive System Diseases, Hepatic Insufficiency, Hepatitis, Chronic, autoimmune disease, autoimmune hepatitis, bile duct disorder, biliary tract disorder, cholangitis, chronic liver failure, hepatitis, immune system disorder, liver disorder, liver failure, primary sclerosing cholangitis | Recruiting | Not stated | 2026-08-19 | NCT05750498 | |
| Dorsal Root Electrical Stimulation in Children With Cerebral Palsy | Brain Damage, Chronic, Muscle Hypertonia, Muscle Spasticity, Neurologic Manifestations, Neuromuscular Manifestations, Pathological Conditions, Signs and Symptoms, Signs and Symptoms, brain disorder, central nervous system disorder, cerebral palsy, muscle tissue disorder, musculoskeletal system disorder, nervous system disorder | Recruiting | Not applicable | 2026-08-11 | NCT07715006 | |
| Molecular Basis of Pediatric Liver Cancer | Digestive System Diseases, Digestive System Neoplasms, Liver Neoplasms, Neoplasms by Histologic Type, Neoplasms by Site, adenocarcinoma, carcinoma, epithelial neoplasm, hepatoblastoma, hepatocellular carcinoma, liver disorder, mixed neoplasm, neoplasm | Recruiting | Not stated | 2026-08-10 | NCT03959800 | |
| Mapping Disease Pathways for Biliary Atresia | Congenital Abnormalities, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Abnormalities, Digestive System Diseases, bile duct disorder, biliary atresia, biliary tract disorder | Recruiting | Not stated | 2026-08-10 | NCT03273049 |