A Study of Patients With Fabry Disease (US Specific)
A Study of Patients With Fabry Disease (US Specific)
Recruiting · NCT06906367 · Registry updated 2026-09-09Clinical trials
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| Trial | Conditions | Status | Phase | Updated | More info | NCT ID |
|---|---|---|---|---|---|---|
| A Study of Patients With Fabry Disease (US Specific) | Brain Diseases, Metabolic, Brain Diseases, Metabolic, Inborn, Cerebral Small Vessel Diseases, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Fabry disease, Lipid Metabolism Disorders, Lipid Metabolism, Inborn Errors, Lysosomal Storage Diseases, Nervous System, Nutritional and Metabolic Diseases, X-linked disease, brain disorder, cardiovascular disorder, central nervous system disorder, cerebrovascular disorder, hereditary disease, inborn errors of metabolism, lysosomal lipid storage disorder, lysosomal storage disease, metabolic disease, nervous system disorder, sphingolipidosis, vascular disorder | Recruiting | Not stated | 2026-09-09 | NCT06906367 |
1 results · Page 1 of 1
Organizations
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| Organizations | Linked trials |
|---|---|
| Amicus Therapeutics | 7 |
8 results · Page 1 of 1
Research sites
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| Research sites | City | Country | Linked trials |
|---|---|---|---|
| Arkansas Children's Hospital | Little Rock | United States | 82 |
| Emory Genetics | Atlanta | United States | 2 |
| Lysosomal and Rare Disorders Research and Treatment Center, Inc. | Fairfax | United States | 6 |
| New York-Presbyterian Morgan Stanley Children's Hospital - Columbia University Medical Center | New York | United States | 1 |
| Renal Disease Research Institute | Dallas | United States | 3 |
| UAB Nephrology Research Clinic at Paula Building | Birmingham | United States | 1 |
| UPMC Children's Hospital of Pittsburgh | Pittsburgh | United States | 70 |
| Washington University School of Medicine | St Louis | United States | 895 |